CompetitionEven with competition, volixibat is seen as well-positioned in large rare diseases, with its potential to differentiate on efficacy and benefit from market developments.
Market DynamicsMirum's development strategy focuses on drugs with proven science but deemed insignificant by big pharma, underscoring the team's disciplined financial approach.
Pipeline RiskVolixibat is undergoing two late-stage trials in primary sclerosing cholangitis and primary biliary cholangitis, which could initiate the next phase of growth for Mirum.