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RARE Stock Chart & Stats
$26.46
-$0.16(-0.59%)
At close: 4:00 PM EDT
$26.46
-$0.16(-0.59%)
Day’s Range― - ―
52-Week Range$12.73 - $39.89
Previous CloseN/A
Volume170.99K
Average Volume (3M)5.04M
Market Cap
$1.57B
Enterprise Value$4.31B
Total Cash (Recent Filing)$292.00M
Total Debt (Recent Filing)$1.20B
Price to Earnings (P/E)―
Beta1.44
Next Earnings
Nov 04, 2026EPS Estimate
-1.11Next Dividend Ex-DateN/A
Dividend YieldN/A
Share Statistics
EPS (TTM)-5.84
Shares Outstanding98,588,875
10 Day Avg. Volume3,678,105
30 Day Avg. Volume5,038,245
Financial Highlights & Ratios
PEG Ratio0.54
Price to Book (P/B)-28.35
Price to Sales (P/S)3.37
P/FCF Ratio-4.80
Enterprise Value/Market Cap2.75
Enterprise Value/Revenue6.01
Enterprise Value/Gross Profit7.23
Enterprise Value/Ebitda-9.11
Forecast
1Y Price Target
$26.25Price Target Upside-0.79% Downside
Rating ConsensusModerate Buy
Number of Analyst Covering21
EPS Forecast (FY)-4.62
Revenue Forecast (FY)$751.44M
Bulls Say, Bears Say
Bulls Say
Revenue Scale And Gross MarginsRapid revenue expansion combined with consistently high gross margins indicates strong economics in the commercial rare-disease portfolio. This gives Ultragenyx meaningful gross profit to reinvest in launches and pipeline programs, although operating costs currently absorb those gains.
FDA Approvals And Non-dilutive CapitalFAYUVI approval expands the commercial rare-disease portfolio while the associated voucher monetization provides substantial non-dilutive capital. This demonstrates that regulatory success can create both product opportunities and funding resources for operations, launches, and future pipeline investment.
Commercial Growth And Cost DisciplineRecord quarterly revenue and broad product growth show increasing commercial traction across the portfolio, while planned expense reductions could improve operating leverage. If double-digit growth and disciplined spending continue, the company has a clearer route toward its stated 2027 profitability objective.
Bears Say
Persistent Losses And Cash BurnLarge recurring cash outflows mean Ultragenyx is not yet self-funding its operations despite revenue growth and high gross margins. Continued losses can require external financing or asset monetization, potentially limiting investment flexibility and making the path to profitability dependent on substantial improvement.
Negative Equity And Leverage RiskNegative equity and the reported debt increase materially weaken financial flexibility. A more leveraged capital structure can constrain spending choices, increase refinancing exposure, and leave fewer balance-sheet resources available to absorb clinical setbacks or slower-than-planned product adoption.
Pipeline Execution And Approval DependenceThe Aspire failure highlights the binary risk of developing therapies for rare and ultra-rare diseases, where a single late-stage setback can reduce pipeline value and force resource reallocation. Near-term growth plans also remain exposed to uncertain regulatory and clinical outcomes.
RARE FAQ
What was Ultragenyx Pharmaceutical’s price range in the past 12 months?
Ultragenyx Pharmaceutical lowest stock price was $12.73 and its highest was $39.89 in the past 12 months.
What is Ultragenyx Pharmaceutical’s market cap?
Ultragenyx Pharmaceutical’s market cap is $1.57B.
When is Ultragenyx Pharmaceutical’s upcoming earnings report date?
Ultragenyx Pharmaceutical’s upcoming earnings report date is Nov 04, 2026 which is in 13 days.
How were Ultragenyx Pharmaceutical’s earnings last quarter?
Ultragenyx Pharmaceutical released its earnings results on Aug 04, 2026. The company reported -$0.9 earnings per share for the quarter, beating the consensus estimate of -$1.218 by $0.318.
Is Ultragenyx Pharmaceutical overvalued?
According to Wall Street analysts Ultragenyx Pharmaceutical’s price is currently Overvalued.
Does Ultragenyx Pharmaceutical pay dividends?
Ultragenyx Pharmaceutical does not currently pay dividends.
What is Ultragenyx Pharmaceutical’s EPS estimate?
Ultragenyx Pharmaceutical’s EPS estimate is -1.11.
How many shares outstanding does Ultragenyx Pharmaceutical have?
Ultragenyx Pharmaceutical has 98,588,875 shares outstanding.
What happened to Ultragenyx Pharmaceutical’s price movement after its last earnings report?
Ultragenyx Pharmaceutical reported an EPS of -$0.9 in its last earnings report, beating expectations of -$1.218. Following the earnings report the stock price went down -3.41%.
Which hedge fund is a major shareholder of Ultragenyx Pharmaceutical?
Currently, no hedge funds are holding shares in RARE
What is the TipRanks Smart Score and how is it calculated?
Smart Score combines eight research factors - such as analyst recommendations, hedge fund trends, and technical indicators - to measure a stock’s outlook. These signals are unified into a single score that reflects bullish or bearish momentum. See detailed methodology
Ultragenyx Pharmaceutical Stock Smart Score
Neutral
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10
Analyst Consensus
Moderate Buy
Average Price Target:
$26.25 (-0.79% Downside)
$26.25 (-0.79% Downside)
Blogger Sentiment
Bullish
RARE Sentiment 88%
Sector Average 67%
Sector Average 67%
Hedge Fund Trend
Decreased
By 85.6K Shares
Last Quarter.
Last Quarter.
Insider Transactions
Sold Shares
Worth $291.9K over
the Last 3 Months
the Last 3 Months
Crowd Wisdom
Very Negative
Last 7 Days ▼ 0.6%
Last 30 Days ▼ 3.7%
Last 30 Days ▼ 3.7%
News Sentiment
Very Bullish
Bullish news 100%
Bearish news 0%
Bearish news 0%
Technicals
SMA
Negative
20 days / 200 days
Momentum
-53.43%
12-Months-Change
Fundamentals
Return on Equity
392.35%
Trailing 12-Months
Asset Growth
-3.24%
Trailing 12-Months
Learn more about TipRanks Smart Score
Company Description
Ultragenyx Pharmaceutical
Ultragenyx Pharmaceutical Inc. is a biopharmaceutical firm dedicated to discovering, developing, and commercializing innovative treatments for rare and ultra-rare genetic conditions. Its operations span North America, Europe, and other international markets. The company's portfolio of marketed biologic products addresses several serious diseases. This includes Crysvita (burosumab), an antibody that targets fibroblast growth factor 23, used to treat X-linked hypophosphatemia and tumor-induced osteomalacia. Mepsevii offers enzyme replacement therapy for both pediatric and adult patients suffering from Mucopolysaccharidosis VII. Dojolvi is available for individuals with long-chain fatty acid oxidation disorders, while Evkeeza (evinacumab) provides a treatment option for homozygous familial hypercholesterolemia. Ultragenyx also boasts a robust pipeline of investigational therapies. Notable candidates include DTX401, an adeno-associated virus 8 (AAV8) gene therapy for glycogen storage disease type Ia, and DTX301, another AAV8 gene therapy aimed at ornithine transcarbamylase deficiency. Other promising developments feature UX143, a human monoclonal antibody for osteogenesis imperfecta; GTX-102, an antisense oligonucleotide designed for Angelman syndrome; UX701, targeting Wilson disease; and UX053, in development for glycogen storage disease type III. To advance its research and development efforts, Ultragenyx Pharmaceutical Inc. maintains strategic collaboration and licensing agreements with numerous partners, such as Kyowa Kirin Co., Ltd., Saint Louis University, REGENXBIO Inc., Bayer Healthcare LLC, GeneTx, Mereo, University of Pennsylvania, Arcturus Therapeutics Holdings Inc., Solid Biosciences Inc., and Daiichi Sankyo Co., Ltd. The company was founded in 2010 and operates from its headquarters in Novato, California.
RARE Earnings Call
Q2 2026
0:00 / 0:00
Earnings Call Sentiment|Positive
Positive overall: the call highlighted record quarterly revenue, broad-based product growth (including Evkeeza +50% YoY), expanding patient counts across multiple geographies, improving cash consumption versus Q1, and clear near-term catalysts (two PDUFAs and a pivotal readout). Management articulated a credible path to profitability in 2027 with expense discipline and potential non-dilutive PRV monetization. Offsetting risks include a sizable operating loss and expense run-rate, reliance on binary regulatory outcomes, an unmet primary outcome for setrusumab requiring possible new trials, and readout/regulatory uncertainty for GTX-102, but these are framed as manageable and addressable within management's plan.View all RARE earnings summariesRARE Stock 12 Month Forecast
Average Price Target
$26.25
▼(-0.79% Downside)
Technical Analysis
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Ownership Overview
3.94% Insiders
19.35% Mutual Funds
0.78% Other Institutional Investors
54.79% Public Companies and Individual Investors









