PTC Therapeutics
PTC Therapeutics, Inc. is a biopharmaceutical company focused on the discovery, development, and commercialization of innovative medicines to treat rare diseases and other serious conditions. The company operates primarily in the biotechnology sector, targeting genetic disorders with a core emphasis on translational medicine. PTC Therapeutics is known for its lead products, including Translarna™ (ataluren), which is designed to treat certain types of Duchenne muscular dystrophy, and Emflaza™ (deflazacort), a corticosteroid for the treatment of Duchenne muscular dystrophy in patients 5 years and older.