Clinical TrialsPTC Therapeutics announced the Phase II CardinALS clinical trial of utreloxastat in ALS failed to meet its primary endpoint of slowing disease progression.
Financial PerformancePTC Therapeutics' expected share price return is projected to be negative.
Regulatory ChallengesThe Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has maintained their negative opinion on the renewal of the marketing authorization of Translarna, which should be ratified by the European Commission and will ultimately result in Translarna being withdrawn from the EU market.