Market ExpansionMitapivat, the lead asset of Agios, is expected to have three approved indications by the end of 2026, expanding its potential market significantly.
Product DevelopmentMitapivat is considered a pipeline-in-a-product with potential for two new and larger label expansions by 2026 in thalassemia and sickle cell disease.
Regulatory ProgressThe regulatory process for mitapivat is progressing ex-US, including in the Gulf Cooperation Council region, which represents a significant opportunity in thalassemia.