Strong Financial Position
Agios has approximately $1.4 billion in cash, ensuring financial independence to fund new approvals, product launches, and pipeline advancement.
PYRUKYND Commercialization Plans
Potential approval and launch of PYRUKYND for thalassemia in the U.S. are expected in September 2025, with sickle cell disease approval anticipated in 2026.
Positive Phase 3 Trial Results
Announced positive top-line results from The ACTIVATE-Kids Phase 3 trial and successful completion of enrollment for the Phase 3 RISE UP study.
Pipeline Advancements
Plans to complete enrollment in Phase 2b study for tebapivat in MDS and initiate a Phase 2 study in sickle cell disease by mid-2025.
Strategic Corporate Development
Hiring of Krishnan Viswanadhan as Chief Corporate Development and Strategy Officer to maximize asset potential and explore expansion opportunities.