Clinical TrialsMIRM announced positive data from the interim analyses of its Phase 2b trials of volixibat in PBC and PSC, showing statistically significant improvements in pruritus vs. placebo.
Drug ApprovalThe FDA has approved a label expansion of LIVMARLI for the treatment of cholestatic pruritus in PFIC patients, now including those aged 12 months and older.
Revenue GrowthMirum Pharmaceuticals remains on track to hit its revenue guidance of $310-$320M with several recent wins across its pipeline.