Financial MilestonesSangamo expects to receive $50M in upfront license fees and milestones and is eligible to earn up to $1.9B in milestones, plus tiered royalties on potential net sales.
Partnerships And CollaborationsThe Genentech partnership reinforces confidence in the potential for Sangamo's zinc finger (ZF) epigenetic regulation and novel adeno-associated virus (AAV) capsid delivery platforms.
Pipeline And Clinical TrialsPositive top-line data emerged from the Phase 3 trial evaluating giroctogene fitelparvovec, a one-time gene therapy being developed in collaboration with Pfizer in hemophilia A.